The progression of myotonic dystrophy type 1 (DM1) differs according to sex and age at symptom onset, a four-year follow-up ...

Usually a DIY project solves a family problem, but columnist Betty Vertin now wonders if her creative efforts contributed to an injury.

Columnist Shalom Lim celebrates a new beginning in a new job, where his mission to serve fellow patients with muscular ...

So we have to change society. It’s a tall order, but it’s been done over and over again throughout history. It starts with a ...

CHMP upheld earlier opinions that Translarna is not of significant benefit to DMD due to nonsense mutations; European ...

Capricor Therapeutics started its rolling submission seeking FDA approval of its DMD therapy deramiocel for heart muscle ...

Hurricanes in the southeastern U.S. prompt columnist Robin Stemple, who has FSHD, to consider his emergency preparedness plan ...

Treatment with antimiRs, an RNA-based therapy approach, was able to correct molecular defects in a cell model of myotonic dystrophy type 1 (DM1) — a form of muscular dystrophy — according to the ...

Treatment with an RNA-based therapy approach was found to correct molecular defects in a cell model of myotonic dystrophy ...

Betty Vertin is a mother and writer living in rural Hastings, Nebraska, with her husband and seven children. Betty is a caregiver to three sons, Max, Rowen, and Charlie. Her oldest was diagnosed with ...