Usually a DIY project solves a family problem, but columnist Betty Vertin now wonders if her creative efforts contributed to an injury.

The progression of myotonic dystrophy type 1 (DM1) differs according to sex and age at symptom onset, a four-year follow-up ...

Columnist Shalom Lim celebrates a new beginning in a new job, where his mission to serve fellow patients with muscular ...

So we have to change society. It’s a tall order, but it’s been done over and over again throughout history. It starts with a ...

CHMP upheld earlier opinions that Translarna is not of significant benefit to DMD due to nonsense mutations; European ...

Capricor Therapeutics started its rolling submission seeking FDA approval of its DMD therapy deramiocel for heart muscle ...

Hurricanes in the southeastern U.S. prompt columnist Robin Stemple, who has FSHD, to consider his emergency preparedness plan ...

The Critical Path Institute will lead a new task force to advance the development of therapies for limb-girdle muscular ...

Treatment with an RNA-based therapy approach was found to correct molecular defects in a cell model of myotonic dystrophy ...

I sat in the front row of the football stadium, watching my second-oldest son, Chance, 17, play football. It’s his senior year, and I’ve been front and center at each game. The rows behind me were ...

Bionews, Inc., the parent company of this site, has partnered with the following nonprofit advocacy organizations to help further the mission of ensuring that patients and caregivers are able to get ...